Summary:
- The FDA has approved a new use for the drug leucovorin, which is typically used to help counteract the side effects of certain cancer treatments.
- This new approval is for the treatment of a rare genetic condition called folate receptor alpha-positive cerebral folate deficiency (FRα-positive CFD), which can cause developmental delays and neurological problems in children.
- The drug works by helping to restore normal folate levels in the brain, which can improve symptoms and cognitive function in patients with this condition.